Tag Archives: Medicine

Gene-silencing: ‘New class’ of medicine reverses disease porphyria

Doctors have used a new type of medicine called “gene silencing” to reverse a disease that leaves people in crippling pain. The condition, acute intermittent porphyria, also causes paralysis and is fatal in some cases. The novel approach fine-tunes the genetic instructions locked in our DNA. Doctors say they are “genuinely surprised” how successful it… Read More »

Precision medicine for pediatric cancer

Research performed over the last several decades has led to an increased understanding of the genetics of cancer. The clinical application of this knowledge for pediatric cancer has lagged behind studies performed for adults. In a perspectives article published in the journal Science, Dr. Jaclyn Biegel, from Children’s Hospital Los Angeles, and Dr. Alejandro Sweet-Cordero,… Read More »